The FDA has cleared the IND for Ensoma's EN-374, targeting X-linked chronic granulomatous disease (X-CGD), a rare genetic ...

Abeona’s deal value is in line with recent voucher sale transactions amid uncertain times in rare disease drug development.

US President Donald Trump has signed an executive order telling drugmakers to cut prices to 'most favoured nation' pricing.

Mobile healthcare, web-based tech, and wearables are all contributing to a clinical trials landscape that puts the patient ...

Orphan drug developers face significant difficulties when navigating market access frameworks in Europe. Could greater use of ...

The European Commission (EC) has granted orphan drug designation to Biodexa Pharmaceuticals’ oral tablet formulation of ...

The Trump administration has introduced legislation outlining plans for deep cuts to Medicaid, possibly impacting millions of ...

AI and machine learning can transform fragmented and unstructured healthcare data. But how do you refine it into useful, ...