The goals of a Phase 2 clinical trial are to determine if the treatment is effective and to gather more safety data. Researchers use the data from Phase 2 trials to refine their research questions ...

With approval to proceed, the Phase II trial (NCT06092034) of RP-A501 for Danon disease restarts under an optimized dosing and immunomodulatory strategy.

Key Facts Clinical trials move through four structured phases, from safety testing to long-term effects. Adaptive, basket, and umbrella trials are making cancer research faster and more flexible.

Following FDA IND clearance for neuropathic pain, the Company is preparing to initiate its U.S. Phase 2a trial in Q4 2025 MIAMI, FL / ACCESS Newswire / August 19, 2025 / MIRA Pharmaceuticals, Inc.

Phase 1 Trials There is little ethical discourse and few publications of phase 1 trials involving healthy volunteers. [17, 18] Phase 1 clinical trials are the gatekeepers for all clinical research.

Historically, more than half of patients with GM2 gangliosidosis need to be fed via IV between 13 and 18 months of age. In ...

MIRA Pharmaceuticals (MIRA) announced the completion of the Single Ascending Dose portion of its ongoing Phase 1 clinical trial evaluating oral ...

The trial aims to assess the regimen over a 90-day period for those with a presumptive diagnosis of the condition.

African Health Research Institute in Durban, and the National Institute for Communicable Diseases in Johannesburg, South Africa. This Phase 1, first-in-human clinical trial will enroll approximately ...

LOS ANGELES-- (BUSINESS WIRE)-- Pelage Pharmaceuticals, a clinical-stage regenerative medicine company, today announced positive results from its Phase 2a clinical trial of PP405 — a topical ...

Dr. Shamoo's critique reveals the essential hypocrisy of the biomedical research enterprise in plying largely poor healthy individuals with money to participate in risky phase 1 clinical trials ...